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Al patrulea Ură Dependenta de cost per averted loss of ambulation dmd neîndemânatic alarma gazdă

PDF) Cost-Effectiveness Analysis of Diagnosis of Duchenne/Becker Muscular  Dystrophy in Colombia
PDF) Cost-Effectiveness Analysis of Diagnosis of Duchenne/Becker Muscular Dystrophy in Colombia

Consensus on the diagnosis, treatment and follow-up of patients with  Duchenne muscular dystrophy | Neurología (English Edition)
Consensus on the diagnosis, treatment and follow-up of patients with Duchenne muscular dystrophy | Neurología (English Edition)

A new era in the management of Duchenne muscular dystrophy - Korinthenberg  - 2019 - Developmental Medicine & Child Neurology - Wiley Online Library
A new era in the management of Duchenne muscular dystrophy - Korinthenberg - 2019 - Developmental Medicine & Child Neurology - Wiley Online Library

Cardiovascular Disease in Duchenne Muscular Dystrophy: Overview and Insight  Into Novel Therapeutic Targets - ScienceDirect
Cardiovascular Disease in Duchenne Muscular Dystrophy: Overview and Insight Into Novel Therapeutic Targets - ScienceDirect

Drug Discovery of Therapies for Duchenne Muscular Dystrophy - SLAS Discovery
Drug Discovery of Therapies for Duchenne Muscular Dystrophy - SLAS Discovery

Peak functional ability and age at loss of ambulation in Duchenne muscular  dystrophy - Zambon - 2022 - Developmental Medicine & Child Neurology -  Wiley Online Library
Peak functional ability and age at loss of ambulation in Duchenne muscular dystrophy - Zambon - 2022 - Developmental Medicine & Child Neurology - Wiley Online Library

Pig models for Duchenne muscular dystrophy – from disease mechanisms to  validation of new diagnostic and therapeutic concepts - ScienceDirect
Pig models for Duchenne muscular dystrophy – from disease mechanisms to validation of new diagnostic and therapeutic concepts - ScienceDirect

Muscle membrane integrity in Duchenne muscular dystrophy: recent advances  in copolymer-based muscle membrane stabilizers | Skeletal Muscle | Full Text
Muscle membrane integrity in Duchenne muscular dystrophy: recent advances in copolymer-based muscle membrane stabilizers | Skeletal Muscle | Full Text

Briefing Document
Briefing Document

Consensus on the diagnosis, treatment and follow-up of patients with  Duchenne muscular dystrophy | Neurología (English Edition)
Consensus on the diagnosis, treatment and follow-up of patients with Duchenne muscular dystrophy | Neurología (English Edition)

Structure-activity relationships of 2-pyrimidinecarbohydrazides as utrophin  modulators for the potential treatment of Duchenne muscular dystrophy -  ScienceDirect
Structure-activity relationships of 2-pyrimidinecarbohydrazides as utrophin modulators for the potential treatment of Duchenne muscular dystrophy - ScienceDirect

Progressive muscle proteome changes in a clinically relevant pig model of  Duchenne muscular dystrophy | Scientific Reports
Progressive muscle proteome changes in a clinically relevant pig model of Duchenne muscular dystrophy | Scientific Reports

Consensus on the diagnosis, treatment and follow-up of patients with  Duchenne muscular dystrophy | Neurología (English Edition)
Consensus on the diagnosis, treatment and follow-up of patients with Duchenne muscular dystrophy | Neurología (English Edition)

BMI-z scores of boys with Duchenne muscular dystrophy already begin to  increase before losing ambulation: a longitudinal exploration of BMI,  corticosteroids and caloric intake - Neuromuscular Disorders
BMI-z scores of boys with Duchenne muscular dystrophy already begin to increase before losing ambulation: a longitudinal exploration of BMI, corticosteroids and caloric intake - Neuromuscular Disorders

Nutrients | Free Full-Text | Metabogenic and Nutriceutical Approaches to  Address Energy Dysregulation and Skeletal Muscle Wasting in Duchenne  Muscular Dystrophy | HTML
Nutrients | Free Full-Text | Metabogenic and Nutriceutical Approaches to Address Energy Dysregulation and Skeletal Muscle Wasting in Duchenne Muscular Dystrophy | HTML

CRISPR applications for Duchenne muscular dystrophy: From animal models to  potential therapies - Chey - WIREs Mechanisms of Disease - Wiley Online  Library
CRISPR applications for Duchenne muscular dystrophy: From animal models to potential therapies - Chey - WIREs Mechanisms of Disease - Wiley Online Library

The effect of steroid treatment on weight in nonambulatory males with  Duchenne muscular dystrophy - Lamb - 2018 - American Journal of Medical  Genetics Part A - Wiley Online Library
The effect of steroid treatment on weight in nonambulatory males with Duchenne muscular dystrophy - Lamb - 2018 - American Journal of Medical Genetics Part A - Wiley Online Library

Viltolarsen in Japanese Duchenne muscular dystrophy patients: A phase 1/2  study - Komaki - 2020 - Annals of Clinical and Translational Neurology -  Wiley Online Library
Viltolarsen in Japanese Duchenne muscular dystrophy patients: A phase 1/2 study - Komaki - 2020 - Annals of Clinical and Translational Neurology - Wiley Online Library

Pig models for Duchenne muscular dystrophy – from disease mechanisms to  validation of new diagnostic and therapeutic concepts - Neuromuscular  Disorders
Pig models for Duchenne muscular dystrophy – from disease mechanisms to validation of new diagnostic and therapeutic concepts - Neuromuscular Disorders

Frontiers | Adeno-Associated Virus (AAV)-Mediated Gene Therapy for Duchenne  Muscular Dystrophy: The Issue of Transgene Persistence
Frontiers | Adeno-Associated Virus (AAV)-Mediated Gene Therapy for Duchenne Muscular Dystrophy: The Issue of Transgene Persistence

PDF) Deflazacort vs prednisone/prednisolone for maintaining motor function  and delaying loss of ambulation: A post hoc analysis from the ACT DMD trial
PDF) Deflazacort vs prednisone/prednisolone for maintaining motor function and delaying loss of ambulation: A post hoc analysis from the ACT DMD trial

PDF) Genotype characterization and delayed loss of ambulation by  glucocorticoids in a large cohort of patients with Duchenne muscular  dystrophy
PDF) Genotype characterization and delayed loss of ambulation by glucocorticoids in a large cohort of patients with Duchenne muscular dystrophy

Frontiers | Therapeutic Strategies for Dystrophin Replacement in Duchenne  Muscular Dystrophy
Frontiers | Therapeutic Strategies for Dystrophin Replacement in Duchenne Muscular Dystrophy

BMI-z scores of boys with Duchenne muscular dystrophy already begin to  increase before losing ambulation: a longitudinal exploration of BMI,  corticosteroids and caloric intake - Neuromuscular Disorders
BMI-z scores of boys with Duchenne muscular dystrophy already begin to increase before losing ambulation: a longitudinal exploration of BMI, corticosteroids and caloric intake - Neuromuscular Disorders

Prognostic indicators of disease progression in Duchenne muscular  dystrophy: A literature review and evidence synthesis | PLOS ONE
Prognostic indicators of disease progression in Duchenne muscular dystrophy: A literature review and evidence synthesis | PLOS ONE

PDF) Reliability of the walking energy cost test and the six-minute walk  test in boys with Duchenne muscular dystrophy
PDF) Reliability of the walking energy cost test and the six-minute walk test in boys with Duchenne muscular dystrophy

PDF) Comparison of Long-term Ambulatory Function in Patients with Duchenne  Muscular Dystrophy Treated with Eteplirsen and Matched Natural History  Controls
PDF) Comparison of Long-term Ambulatory Function in Patients with Duchenne Muscular Dystrophy Treated with Eteplirsen and Matched Natural History Controls